Dinakar Singh
👤 SpeakerAppearances Over Time
Podcast Appearances
Let's go test it out.
They're doing it.
So fingers crossed.
I think my hope here is that we'll end up with a handful of drugs in the next handful of years that could really help bring back some strength for kids with SMA and other things as well.
That would be amazing because as amazing a life as a daughter has now, she is still fragile.
And when you're fragile, as you get older, things happen.
And so if we can bring back some strength, that will be even more transformative and even more impactful.
So it's exciting stuff.
So a child born and getting the drug close to diagnosis will never show symptoms.
Yeah.
20,000 kids and their families.
Many of the people that we've gotten to know the best over the years are people whose kids are affected by disease because there's a commonality.
And it's devastating for everyone.
Parents who lose their jobs because they keep taking time off and they can't afford the insurance.
I mean, it's just this horrible spiral.
There was a family, the father worked at Walmart.
They had twins with SNA and he just wanted to cry hearing their story.
That is the funny irony with all this stuff.
My parents were both scientists and they would joke that it was such a tragedy that both their kids became Parker's Goldman Sachs.
In some ways,