Dr. David Fajgenbaum

about 20 kids ever, where kids are born with this horrible rare condition where they basically, they're hypotonic, which means their muscles don't work, so they're on feeding tubes, and they're basically bedbound, and they would be bedbound their whole lives.

But there's a drug called DFMO that's been around for a long time that wasn't made for this condition, and it actually is really effective.

So the kids that have been started on DFMO early in life

are standing up, sitting up.

Some of them were even walking the kids that are started later on in life.

Maybe they're feeding tubes out, but they're not quite at the same level they would have been if they were, um, if they were a typical child.

Um, this is why we started this organization is like maybe only a couple dozen kids are going to benefit in the short term.

but maybe a couple hundred are gonna benefit in the longer term, and they're gonna benefit walking to school and running with their siblings and doing things that they wouldn't have been able to do with a drug that wasn't made for their condition.

And so those are the kinds of things that that's just not gonna, in our industry,

a couple dozen kids, no one's gonna take a cheap old drug and work on a couple dozen.

And it's not that they're not gonna work on it, I take that back, because I should really emphasize that there's been amazing work done, because the condition's called Bachman-Bopp, and that's after two doctors, Dr. Bachman and Dr. Bopp, who have done just the most outstanding work in the world to advance treatments for this condition.

But the point being that typically, that's where it would stop, with this doctor and that doctor, they're doing the best they can for these kids.

But us at EveryCure, we're trying to find as many of these as we can.

So that way, to your point, we get the word out.

So if you're a child in some other part of the world and you've got this condition, let's get you diagnosed and let's get you on the medicine.

And then another 4,000 have treatments.

How do you guys sift through all of that?

Yeah.

So we get a score from zero to one for each, every drug against every disease.

So like,